Clinical trial shows gene editing works for β-Thalassaemia, too
via fda.gov
Short excerpt below. Read at the original source.
Almost as soon as researchers started exploring the capabilities of the CRISPR/Cas9 system, they recognized its potential use in targeted gene editing. But the intervening decades have seen slow progress as people worked to determine how to do so in a way that would be safe for use in humans. It was only a little […]